The first treatment has been approved for progeria, Friday, Nov.
A breakthrough medication for the ultra rare genetic disease known as progeria has been approved by the Food and Drug Administration (FDA).— The Progeria Research Foundation (@Progeria) November 20, 2020.Research behind the treatment was largely funded by the Progeria Research Foundation (PRF).
Progeria, also known as Hutchinson-Gilford Progeria Syndrome, has been described by the FDA as a “rare genetic disease that causes premature aging, death and has a debilitating effect on people’s lives.”.